Do you want to read an article? Please log in or register.
Body composition changes and clinical outcomes in pediatric cystic fibrosis during 24 months of lumacaftor ivacaftor therapy based on real-world data
Pulmonary Fibrosis
RECOMMENDED
Related content
RECOMMENDED
Pulmonary Fibrosis
The expanded French compassionate programme for elexacaftor-tezacaftor-ivacaftor use in people with cystic fibrosis without a F508del CFTR variant: a real-world study
★ 2
Recommended by
Dr Martin Frey, Faculty Member
Lancet Respir Med
Burgel PR, Sermet-Gaudelus I, Girodon E, Durieu I, Houdouin V, Audousset C, Macey J, Grenet D, Porzio M, Murris-Espin M, Reix P, Baravalle M, Belleguic C, Mely L, Verhille J, Weiss L, Reynaud-Gaubert M, Mittaine M, Hamidfar R, Ramel S, Cosson L, Douvry B, Danner-Boucher I, Foucaud P, Roy C, Burnet E, Raynal C, Audrezet MP, Da Silva J, Martin C, French Cystic Fibrosis Reference Network study group
doi: 10.1016/S2213-2600(24)00208-X
RECOMMENDED
Pulmonary Fibrosis
Outcomes of a cross-sectional ultrasound- based study of cystic fibrosis related liver disease: A real world experience
★ 1
Recommended by
Dr Martin Frey, Faculty Member
J Cyst Fibros
Kurkal K, Kuek SL, Herath D, Ong C, Harrison J, Cooney H, Poulter C, Oliver M
doi: 10.1016/j.jcf.2024.06.008
Pulmonary Fibrosis
Real-World Effectiveness and Safety of Elexacaftor/Tezacaftor/Ivacaftor in Cystic Fibrosis Patients with Phe508del -Gating and -Residual Function Genotypes
Respir Med
Salvatore D, Iacotucci P, Pepe A, Terminiello A, Majo F, Carnovale V, Vitullo P, Messore B, Parisi GF, Calderazzo MA, Leonetti G, Terlizzi V
doi: 10.1016/j.rmed.2025.108221
Pulmonary Fibrosis
LONGITUDE: An observational study of the long-term effectiveness of elexacaftor/tezacaftor/ivacaftor in people aged ≥12 years with cystic fibrosis using data from the United Kingdom Cystic Fibrosis Registry - 2-year analysis
J Cyst Fibros
Vega-Hernandez G, MacGregor G, Wilfin A, Adams F, Haugh C, Baxter CA, Wöhling H, Clarke SL, Charman SC, Carr SB
doi: 10.1016/j.jcf.2025.04.012
RECOMMENDED
Lung Cancer
Clinical implementation of next-generation sequencing testing and genomically-matched therapy: a real-world data in a tertiary hospital
★ 1
Recommended by
Dr Martin Frey, Faculty Member
★ 1
Recommended by
Dr Marcus Hesse, Faculty Member
Sci Rep
Kim JW, Na HY, Lee S, Kim JW, Suh KJ, Kim SH, Kim YJ, Lee KW, Lee JS, Kim J, Hwang JH, Hwang K, Kim CY, Kim YB, Ahn S, Lee KS, Kim H, Lee HS, Park SY, Choe G, Kim JH, Chung JH
doi: 10.1038/s41598-024-84909-9
RECOMMENDED
Further Publications
Effects on growth, weight and body composition after CFTR modulators in children with cystic fibrosis
★ 1
Recommended by
Dr Martin Frey, Faculty Member
★ 1
Recommended by
Dr Marcus Hesse, Faculty Member
Pediatr Pulmonol
López Cárdenes CM, Merino Sánchez-Cañete A, Vicente Santamaría S, Gascón Galindo C, Merino Sanz N, Tabares González A, Blitz Castro E, Morales Tirado A, Garriga García M, López Rozas M, Ramos Riesgo T, Álvarez Beltrán M, Gutiérrez Martínez JR, Suárez González M, García Romero R, De la Mano Hernández A, Muñoz Codoceo MR, Martín Fernández C, Tutau Gómez C, Torcuato Rubio E, Ortiz Pérez P, Loverdos Eseverri I, García Volpe C, Salcedo Lobato E, Martín Rivada A, Castro Millan AM, Del Brio Castillo R, Sierra San Nicolás S, Murray Hurtado M, Crehuá Gaudiza E, Medina Martínez M, González Jiménez D, y grupo de trabajo de FQ y páncreas de la SEGHNP
doi: 10.1002/ppul.27272
RECOMMENDED
Pulmonary Fibrosis
First real-world study of fetal therapy with CFTR modulators in cystic fibrosis: Report from the MODUL-CF study
★ 2
Recommended by
Dr Martin Frey, Faculty Member
★ 1
Recommended by
Dr Marcus Hesse, Faculty Member
J Cyst Fibros
Bonnel AS, Bihouée T, Ribault M, Driessen M, Grèvent D, Foissac F, Truong NH, Benhamida M, Arnouat B, Borghese R, Chedevergne F, Couderc-Kohen L, da Silva J, Grenet D, Houdouin V, Le A, Marchal S, Deneuville E, Pouradier D, Rousseau V, Treluyer JM, Francart A, Steffann J, Reix P, Benaboud S, Mamzer MF, Ville Y, Martin C, Burgel PR, Sermet-Gaudelus I, MODUL-CF study group
doi: 10.1016/j.jcf.2025.03.009
RECOMMENDED
Sleep Apnea
Real-world data on polysomnography- and patient-reported outcomes in hypoglossal nerve stimulation and auto-titrating positive airway pressure therapy for obstructive sleep apnea
★ 1
Recommended by
Dr Martin Frey, Faculty Member
★ 1
Recommended by
Dr Marcus Hesse, Faculty Member
Respir Med
Pordzik J, Ludwig K, Seifen C, Ruckes C, Huppertz T, Bahr-Hamm K, Hackenberg B, Matthias C, Gouveris H
doi: 10.1016/j.rmed.2024.107750
RECOMMENDED
Pulmonary Fibrosis
Long-term impact of ivacaftor on mortality rate and health outcomes in people with cystic fibrosis
★ 2
Recommended by
Dr Martin Frey, Faculty Member
★ 2
Recommended by
Dr Marcus Hesse, Faculty Member
Thorax
Merlo CA, Thorat T, DerSarkissian M, McGarry LJ, Nguyen C, Gu YM, Healy J, Rubin JL, Brookhart MA
doi: 10.1136/thorax-2023-220558